Author information:
(1)1] The Center for Gene Therapy, Nationwide Children's Hospital, The Ohio 
State University, Columbus, Ohio, USA. [2].
(2)Section of Microbiology and Medical Genetics, Department of Medical Sciences, 
University of Ferrara, Ferrara, Italy.
(3)Department of Proteomics and Nanobiotechnology, School of Biotechnology, KTH 
Royal Institute of Technology, Stockholm, Sweden.
(4)Department of Neurology, Washington University School of Medicine, St. Louis, 
Missouri, USA.
(5)The Center for Gene Therapy, Nationwide Children's Hospital, The Ohio State 
University, Columbus, Ohio, USA.
(6)1] Center for RNA Biology, The Ohio State University, Columbus, Ohio, USA. 
[2] Department of Molecular and Cellular Biochemistry, The Ohio State 
University, Columbus, Ohio, USA.
(7)Department of Neuroscience, University of Messina and Centro Clinico Nemo 
Sud, Messina, Italy.
(8)Bambino Gesù Children's Hospital, Rome, Italy.
(9)Centre for Comparative Genomics, Murdoch University, Perth, Western 
Australia, Australia.
(10)1] The Center for Gene Therapy, Nationwide Children's Hospital, The Ohio 
State University, Columbus, Ohio, USA. [2] Department of Pediatrics, The Ohio 
State University, Columbus, Ohio, USA.
(11)Division of Biomedical Informatics, Department of Computer Science, 
University of Kentucky Lexington, Kentucky, USA.
(12)Department of Human Genetics, The University of Utah School of Medicine, 
Salt Lake City, Utah, USA.
(13)1] The Center for Gene Therapy, Nationwide Children's Hospital, The Ohio 
State University, Columbus, Ohio, USA. [2] Department of Pediatrics, The Ohio 
State University, Columbus, Ohio, USA. [3] Department of Neurology, The Ohio 
State University, Columbus, Ohio, USA.